Unlocking the Potential of Cell and Gene Therapies MasterClass
Online
Thu, Sep 23, 2021,
09:00
- Fri, Sep 24, 2021
16:30
Central European Time
For price and detailed agenda, visit the site and request the agenda!
Nowadays, for as much as 95% of the 7 000 to 10 000 rare diseases that exist, there are no approved therapies. Of the estimated 400 M people worldwide afflicted with a rare disease, 50% are children. Cell and gene therapies have emerged as a new treatment paradigm for many rare diseases. These novel medicines have the potential to provide long-term therapeutic benefits for patients, however their development is both risky and cost intensive.